A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy (Jewelfish)
An Open-Label Study to Investigate the Safety, Tolerability, and Pharmacokinetics/Pharmacodynamics of Risdiplam (RO7034067) in Adult and Pediatric Patients With Spinal Muscular Atrophy
Sponsor: Hoffmann-La Roche
This PHASE2 trial investigates Spinal Muscular Atrophy and is currently completed. Hoffmann-La Roche leads this study, which shows 49 recorded versions since 2017 — indicating substantial longitudinal coverage. The change history captured here reflects the iterative nature of clinical trial conduct.
Status Flow
Change History
49 versions recorded-
Nov 2025 — Present [monthly]
Completed PHASE2
-
Sep 2025 — Nov 2025 [monthly]
Completed PHASE2
-
Mar 2025 — Sep 2025 [monthly]
Completed PHASE2
Status: Active Not Recruiting → Completed
-
Feb 2025 — Mar 2025 [monthly]
Active Not Recruiting PHASE2
-
Jan 2025 — Feb 2025 [monthly]
Active Not Recruiting PHASE2
▶ Show 44 earlier versions
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Oct 2024 — Jan 2025 [monthly]
Active Not Recruiting PHASE2
-
Sep 2024 — Oct 2024 [monthly]
Active Not Recruiting PHASE2
-
Jul 2024 — Sep 2024 [monthly]
Active Not Recruiting PHASE2
-
Apr 2024 — Jul 2024 [monthly]
Active Not Recruiting PHASE2
-
Jan 2024 — Apr 2024 [monthly]
Active Not Recruiting PHASE2
-
Nov 2023 — Jan 2024 [monthly]
Active Not Recruiting PHASE2
-
Aug 2023 — Nov 2023 [monthly]
Active Not Recruiting PHASE2
-
May 2023 — Aug 2023 [monthly]
Active Not Recruiting PHASE2
-
Feb 2023 — May 2023 [monthly]
Active Not Recruiting PHASE2
-
Nov 2022 — Feb 2023 [monthly]
Active Not Recruiting PHASE2
-
Sep 2022 — Nov 2022 [monthly]
Active Not Recruiting PHASE2
-
Jun 2022 — Sep 2022 [monthly]
Active Not Recruiting PHASE2
-
Mar 2022 — Jun 2022 [monthly]
Active Not Recruiting PHASE2
-
Feb 2022 — Mar 2022 [monthly]
Active Not Recruiting PHASE2
-
Nov 2021 — Feb 2022 [monthly]
Active Not Recruiting PHASE2
-
Sep 2021 — Nov 2021 [monthly]
Active Not Recruiting PHASE2
-
Jun 2021 — Sep 2021 [monthly]
Active Not Recruiting PHASE2
-
Mar 2021 — Jun 2021 [monthly]
Active Not Recruiting PHASE2
-
Jan 2021 — Mar 2021 [monthly]
Active Not Recruiting PHASE2
-
Nov 2020 — Jan 2021 [monthly]
Active Not Recruiting PHASE2
-
Aug 2020 — Nov 2020 [monthly]
Active Not Recruiting PHASE2
-
Jun 2020 — Aug 2020 [monthly]
Active Not Recruiting PHASE2
-
Feb 2020 — Jun 2020 [monthly]
Active Not Recruiting PHASE2
Status: Recruiting → Active Not Recruiting
-
Jan 2020 — Feb 2020 [monthly]
Recruiting PHASE2
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Nov 2019 — Jan 2020 [monthly]
Recruiting PHASE2
-
Oct 2019 — Nov 2019 [monthly]
Recruiting PHASE2
-
Sep 2019 — Oct 2019 [monthly]
Recruiting PHASE2
-
Aug 2019 — Sep 2019 [monthly]
Recruiting PHASE2
-
Jul 2019 — Aug 2019 [monthly]
Recruiting PHASE2
-
Jun 2019 — Jul 2019 [monthly]
Recruiting PHASE2
-
Apr 2019 — Jun 2019 [monthly]
Recruiting PHASE2
-
Mar 2019 — Apr 2019 [monthly]
Recruiting PHASE2
-
Feb 2019 — Mar 2019 [monthly]
Recruiting PHASE2
-
Jan 2019 — Feb 2019 [monthly]
Recruiting PHASE2
-
Dec 2018 — Jan 2019 [monthly]
Recruiting PHASE2
-
Sep 2018 — Dec 2018 [monthly]
Recruiting PHASE2
-
Aug 2018 — Sep 2018 [monthly]
Recruiting PHASE2
-
Jul 2018 — Aug 2018 [monthly]
Recruiting PHASE2
-
Jun 2018 — Jul 2018 [monthly]
Recruiting PHASE2
-
Jan 2018 — Jun 2018 [monthly]
Recruiting PHASE2
-
Aug 2017 — Jan 2018 [monthly]
Recruiting PHASE2
-
May 2017 — Aug 2017 [monthly]
Recruiting PHASE2
-
Mar 2017 — May 2017 [monthly]
Recruiting PHASE2
Status: Not Yet Recruiting → Recruiting
-
Feb 2017 — Mar 2017 [monthly]
Not Yet Recruiting PHASE2
First recorded
Eligibility Summary
No eligibility information available.
Contact Information
- Hoffmann-La Roche
For direct contact, visit the study record on ClinicalTrials.gov .
Study Locations
Basel, Switzerland , Birmingham, United Kingdom , Boston, United States , Bron, France , Essen, Germany , Freiburg im Breisgau, Germany , Genoa, Italy , Ghent, Belgium , Leuven, Belgium , Lille, France and 13 more locations