EPI-743 for Mitochondrial Respiratory Chain Diseases
Emergency Use Protocol for EPI-743 in Acutely Ill Patients With Inherited Mitochondrial Respiratory Chain Disease Within 90 Days of End-of-Life Care
Sponsor: PTC Therapeutics
Listed as NCT01370447, this observational or N/A phase trial focuses on Mitochondrial Diseases and remains ongoing. Sponsored by PTC Therapeutics, it has been updated 29 times since 2026, reflecting substantial change activity. This study adds to the evidence base for this therapeutic area through structured, versioned documentation.
Change History
29 versions recorded-
Sep 2024 — Present [monthly]
No Longer Available
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Jul 2024 — Sep 2024 [monthly]
No Longer Available
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Feb 2024 — Jul 2024 [monthly]
No Longer Available
Status: Completed → No Longer Available · Phase: PHASE2 → None
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Nov 2023 — Feb 2024 [monthly]
Completed PHASE2
Status: Active Not Recruiting → Completed
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Oct 2023 — Nov 2023 [monthly]
Active Not Recruiting PHASE2
▶ Show 24 earlier versions
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Sep 2023 — Oct 2023 [monthly]
Active Not Recruiting PHASE2
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Jul 2023 — Sep 2023 [monthly]
Active Not Recruiting PHASE2
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May 2023 — Jul 2023 [monthly]
Active Not Recruiting PHASE2
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Apr 2023 — May 2023 [monthly]
Active Not Recruiting PHASE2
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Dec 2022 — Apr 2023 [monthly]
Active Not Recruiting PHASE2
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Sep 2022 — Dec 2022 [monthly]
Active Not Recruiting PHASE2
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Jun 2022 — Sep 2022 [monthly]
Active Not Recruiting PHASE2
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Apr 2022 — Jun 2022 [monthly]
Active Not Recruiting PHASE2
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Jan 2022 — Apr 2022 [monthly]
Active Not Recruiting PHASE2
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Nov 2021 — Jan 2022 [monthly]
Active Not Recruiting PHASE2
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Sep 2021 — Nov 2021 [monthly]
Active Not Recruiting PHASE2
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Jun 2021 — Sep 2021 [monthly]
Active Not Recruiting PHASE2
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May 2021 — Jun 2021 [monthly]
Active Not Recruiting PHASE2
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Feb 2021 — May 2021 [monthly]
Active Not Recruiting PHASE2
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Jan 2021 — Feb 2021 [monthly]
Active Not Recruiting PHASE2
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Nov 2020 — Jan 2021 [monthly]
Active Not Recruiting PHASE2
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Sep 2020 — Nov 2020 [monthly]
Active Not Recruiting PHASE2
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Jul 2020 — Sep 2020 [monthly]
Active Not Recruiting PHASE2
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Aug 2019 — Jul 2020 [monthly]
Active Not Recruiting PHASE2
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Aug 2018 — Aug 2019 [monthly]
Active Not Recruiting PHASE2
Status: Unknown Status → Active Not Recruiting
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Jun 2018 — Aug 2018 [monthly]
Unknown Status PHASE2
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Apr 2018 — Jun 2018 [monthly]
Unknown Status PHASE2
Status: Active Not Recruiting → Unknown Status
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Feb 2017 — Apr 2018 [monthly]
Active Not Recruiting PHASE2
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Jan 2017 — Feb 2017 [monthly]
Active Not Recruiting PHASE2
First recorded
Eligibility Summary
No eligibility information available.
Contact Information
- PTC Therapeutics
For direct contact, visit the study record on ClinicalTrials.gov .
Study Locations
Akron, United States, Bremerton, United States, Charlotte, United States, Cleveland, United States, Decatur, United States, Houston, United States, Los Angeles, United States, New York, United States, North Charleston, United States, Orange, United States and 5 more location s